You are currently viewing A lifesaving therapy for children with a rare disease is now the world’s most expensive drug raising questions about access – CNN

A lifesaving therapy for children with a rare disease is now the world’s most expensive drug raising questions about access – CNN

A new gene therapy for the fatal genetic disorder metachromatic leukodystrophy, or MLD, will carry a wholesale price of $4.25 million, its manufacturer announced Wednesday, making it the worlds most … [read more]

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